Rare Disease Day on February 29, 2024

Rare Disease Day on February 29, 2024

Rare Disease Day is a global movement to raise awareness about rare diseases and the challenges faced by those living with them. This day serves as a powerful reminder of the extraordinary resilience and spirit of the individuals worldwide living with a rare disease,...
What have we been up to in 2023?

What have we been up to in 2023?

Every year, we like to provide an update on our projects, offering you insights into what we are working on and what is on the horizon. On November 14th, we hosted an online event for individuals with DRPLA and their family members in which Dr. Silvia Prades gave an...