Did you miss our meeting on December 4? Do not worry—we have got you covered! Dr Silvia Prades recorded her presentation to allow more people to learn about our work and updates. This talk included updates on our organization, the DRPLA Natural History and Biomarkers...

The International Congress for Ataxia Research (ICAR) was held in London on November 12-15. This was the biggest gathering of people interested in ataxia, with 600 attendees from 32 countries. The audience included scientists, clinicians and representatives from...

For the third year in a row, we organized the CureDRPLA Research Conference in Boston to bring together scientists funded by us, healthcare professionals and representatives of pharmaceutical companies. At these meetings, we review the past year’s progress and invite...

CureDRPLA was founded in November 2019 and in light of our forthcoming founding anniversary, we have prepared an impact report to summarize our work and milestones. In this report you will find a summary of our achievements to date and our goals for the next 5 years....

Last week, Dr Silvia Prades attended a conference to find out more about the latest work on rare diseases and how the medicines regulatory framework is expected to change in the coming years to facilitate research and approval of treatments for rare conditions like...